Phase III, Single-arm, Open-label, International, Multi-centre Study to Evaluate the Efficacy and Safety of Lomitapide in Paediatric Patients with Homozygous Familial Hypercholesterolaemia (HoFH) on Stable Lipid-lowering Therapy
عنوان الدراسة
Phase III, Single-arm, Open-label, International, Multi-centre Study to Evaluate the Efficacy and Safety of Lomitapide in Paediatric Patients with Homozygous Familial Hypercholesterolaemia (HoFH) on Stable Lipid-lowering Therapy
داعم الدراسة
Amryt Pharmaceuticals DAC
دواء الدراسة
LOMITAPIDE
رقم بروتوكول الدراسة
APH-19
حالة الدراسة
Ongoing
موقع الدراسة
King Abdulaziz Medical City NG (Riyadh)
مرحلة الدراسة
3
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