A Phase 3, Randomized, Double-Blind, Placebo-Controlled, Multinational Clinical Study to Evaluate the Efficacy and Safety of 2.0 mg/kg/Week and 2.0 mg/kg/Every Other Week BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome)
عنوان الدراسة
A Phase 3, Randomized, Double-Blind, Placebo-Controlled, Multinational Clinical Study to Evaluate the Efficacy and Safety of 2.0 mg/kg/Week and 2.0 mg/kg/Every Other Week BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome)
داعم الدراسة
BioMarin Pharmaceutical Inc.
دواء الدراسة
BMN 110
رقم بروتوكول الدراسة
MOR-004
حالة الدراسة
Completed
موقع الدراسة
KFSH & RC-R
مرحلة الدراسة
3
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