"A PHASE 2/3, MULTICENTER, MULTINATIONAL, OPEN-LABEL STUDY TO EVALUATE THE EFFICACY AND SAFETY OF ALXN1101 IN NEONATES WITH MOLYBDENUM COFACTOR DEFICIENCY (MOCD) TYPE A"
عنوان الدراسة
"A PHASE 2/3, MULTICENTER, MULTINATIONAL, OPEN-LABEL STUDY TO EVALUATE THE EFFICACY AND SAFETY OF ALXN1101 IN NEONATES WITH MOLYBDENUM COFACTOR DEFICIENCY (MOCD) TYPE A"
داعم الدراسة
Alexion
دواء الدراسة
ALXN1101( Cyclic pyranopterin monophosphate monohydrobromide dihydrate)
رقم بروتوكول الدراسة
ALXN1101-MCD-202
حالة الدراسة
Terminated
موقع الدراسة
KFMC
مرحلة الدراسة
2/3
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