"A PHASE 2/3, MULTICENTER, MULTINATIONAL,OPEN-LABEL STUDY TO EVALUATE THE EFFICACY ANDSAFETY OF ALXN1101 IN NEONATES WITH MOLYBDENUMCOFACTOR DEFICIENCY (MOCD) TYPE A"
عنوان الدراسة
"A PHASE 2/3, MULTICENTER, MULTINATIONAL,OPEN-LABEL STUDY TO EVALUATE THE EFFICACY ANDSAFETY OF ALXN1101 IN NEONATES WITH MOLYBDENUMCOFACTOR DEFICIENCY (MOCD) TYPE A"
داعم الدراسة
Alexion
دواء الدراسة
ALXN1101( Cyclic pyranopterin monophosphate monohydrobromide dihydrate)
رقم بروتوكول الدراسة
ALXN1101-MCD-202
حالة الدراسة
Ongoing
موقع الدراسة
King Fahad Medical City (Riyadh)
مرحلة الدراسة
2b
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